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靶点针对疾病信息7(本栏目收费,不能显示细节,电话13136136841)
靶点针对疾病信息
TARGNAME
Dystrophin nonsense mutant (DMD)
INDICATI
Phase 3 Epilepsy/seizure [ICD-11: 8A61-8A6Z]
INDICATI
Phase 3 Eye anterior segment structural developmental anomaly [ICD-11: LA11]
INDICATI
Phase 3 Lysosomal disease [ICD-11: 5C56]
INDICATI
Phase 3 Muscular dystrophy [ICD-11: 8C70]